Amicus Therapeutics Highlights New Phase 3 Fabry Data and Preclinical Pompe Data at WORLDSymposium™ 2016
New Phase 3 Data for Migalastat for Fabry Disease Demonstrate Persistence of Positive Renal and Cardiac Effects and Substrate Reduction in Important Kidney Cell Type (Podocytes)
Preclinical Proof-of-Concept Data Informed Ongoing Clinical Study
of Novel Pompe Treatment Paradigm
SAN DIEGO and CRANBURY, N.J., March 01, 2016 -- Amicus Therapeutics (FOLD), a biotechnology company at the forefront of therapies for rare and orphan diseases, today announced new positive data from both of its Phase 3 studies of the oral small molecule pharmacological chaperone migalastat HCl (“migalastat”) for Fabry disease at WORLDSymposium™ 2016 in San Diego, California. The Company is also presenting additional proof-of-concept data for its novel product candidate (ATB200/AT2221) for Pompe disease.
- Published: 02 March 2016
- Written by Editor